19. Investigative Treatment Division

The main goal of the research of this division is innovation of a new strategy for cancer diagnosis, treatment and prevention. For this purpose, currently three projects are on going.

New Strategy for Gene Therapy

About 15% of mutations affecting tumor suppressor genes are reported to be mutations disturbing RNA splicing. These mutations often result in a loss of gene function but sometimes also result in production of a deleterious product, a dominant negative effect. In the latter case, such as p53 gene mutation, supplementation with a wild type gene product is not enough to overcome the effect of mutation; reduction of the mutated product is necessary. However, so far no strategy for suppressing a splicing mutation has been established. A series of mutant U1snRNA expression vectors was constructed, which have various base substitutions in the 5'-portion that hybridize with a splice-donor site of pre-mRNA, and some of the mutations were found to effectively suppress the splice-donor site mutation in a model system using Nagase analbuminemic rats.(37) These expression vectors did not alter cell growth, morphology or anchorage independence in cultured mammalian cells. This new strategy for manipulation of pre-mRNA splicing should be very promising also for the treatment of diseases caused by RNA tumor viruses. In addition, the pattern of alternative splicing often changes during carcinogenesis in various genes such as fibronectin troponiyosin, CD44, k-ras, and DCC. These changes in alternative splicing are deeply involved in carcinogenesis. The present strategy for manipulations of pre-mRNA splicing will open a new field of research on tumor biology and cancer therapy.

Analysis of Minute Lesions of the Colon

In order to understand the carcinogenesis process completely, identification of very early minute lesions which are potentially precursors of advanced carcinomas is important. Aberrant crypt foci (ACF) were extensively studied and activation of K-ras codons 12 and 13 was proved to be very frequent even in a very small ACF, less than 0.1 mm in diameter. The incidence was increased to about 90% for the lesions 0.5 mm to 3 mm in diameter. Cell proliferation in ACF was studied in rat colon. Increased cell proliferation in ACF was proved by the mitotic index, BrdU labeling index and proliferating cell nuclear antigen (PCNA) staining and this was also true even in ACF consisting of one crypt.(33) The same increased cell proliferation in ACF was also demonstrated in human ACF by PCNA staining. Histologically, small ACF, less than 0.1 mm in diameter, were hyperplastic. The adenomatous component became prominent in the larger ACF. Histological examination of larger ACF, 0.1 mm to 3 mm in diameter, revealed that about 1/2 of the focus is hyperplastic, 1/5 is a mixture of hyperplasia and adenoma and the remaining 1/3 is adenoma. PCNA staining was clearly stronger in adenomatous lesions than in hyperplastic lesions. This tendency was clear even in ACF consisting of a hyperplastic portion and an adeno-matous portion. Therefore, an ACF seemed to be formed as a hyperplastic lesion through K-ras activation and to progress into an adenomatous lesion through so far unidentified genetic changes with further increased cell proliferation. Macroscopically normal mucosa was examined for a mutant K-ras gene by using the enriched polymerase chain reaction. The mutant K-ras gene was detected in about 10% of the samples of normal mucosa from the colon of patients with colorectal cancer.(34) The origin of the mutant K-ras gene is not clear at present but most likely these mutant k-ras genes represent the existence of very minute neoplastic lesions such as ACF. Evaluation of detection of mutant K-ras gene as a biomarker of the risk for colorectal cancer is under investigation.

Implication of Nitric Oxide Synthase in Clinical Features of Cancer Patients

Nitric oxide is a relatively newly identified signaling molecule in various biological processes.(25-31) Therefore, it could be one of the new target molecules for cancer therapy. Paclitaxel is one of the most promising cancer chemotherapeutic agents and many clinical trials are ongoing. One serious adverse effect of it is hypotension. Taxol has been shown to have a bacterial lipopolysaccharide-like action. Taxol was found to induce nitric oxide synthase mRNA in macrophages and endothelial cells and this induction was considered to be one of the mechanisms of hypotension caused by the drug. A study on the induction of nitric oxide synthase in patients administered paclitaxel is ongoing. Induction of nitric oxide synthase is also being studied in connection with the adverse effects of vincalkaloides on the nervous system. The contribution of nitric oxide synthase to diarrhea, lung fibrosis and hemorrhagic diathesis is also being investigated.


List of papers from this division
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